Hey, wait a second. What about Roche’s PhIII hemophilia A drug?
Largely overshadowed by BioMarin’s potentially landmark gene therapy results for hemophilia A, a group from Roche’s Chugai subsidiary turned up at the same scientific conference this week to spotlight updated evidence that their bispecific antibody emicizumab dramatically slashed the rate of bleeding episodes in a small but significant clinical trial.
Emicizumab, formerly ACE910, has been repeatedly tapped by Roche’s Daniel O’Day as a top blockbuster candidate for the pharma giant. But now the injectable will have to compete for attention with BioMarin and rivals who are working with once-and-done gene therapies that promise to fix the biologic dysfunction that prevents normal clotting in patients’ blood.
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