Anthony Saleh, miRecule CEO

Sanofi li­cens­es a pre­clin­i­cal ge­net­ic dis­ease drug from an un­known biotech spun out of the NIH

In a new deal Tues­day morn­ing, Sanofi is jump­ing in­to the an­ti­body-RNA con­ju­gate (ARC) space and el­e­vat­ing a lit­tle-known pri­vate biotech in­to the spot­light.

Sanofi is li­cens­ing a pre­clin­i­cal ARC can­di­date from Gaithers­burg, MD-based miRecule that’s de­signed to treat a ge­net­ic mus­cle dis­ease known as fa­cioscapu­lo­humer­al mus­cu­lar dy­s­tro­phy, or FSHD. Sanofi is get­ting ex­clu­sive world­wide rights for the pro­gram, known as MC-DX4, while miRecule gets an up­front and near-term mile­stones of about $30 mil­lion.

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