An­a­lysts see promise in Fi­bro­Gen's ear­ly Duchenne study — now they want to see a piv­otal tri­al

Apart from Pfiz­er $PFE, Fi­bro­Gen $FGEN on Fri­day al­so pre­sent­ed ear­ly da­ta on its drug for Duchenne mus­cu­lar dy­s­tro­phy.

The drug, pam­revlum­ab, is a mon­o­clon­al an­ti­body to con­nec­tive tis­sue growth fac­tor (CT­GF) cur­rent­ly un­der de­vel­op­ment as a treat­ment for non-am­bu­la­to­ry DMD pa­tients, id­io­path­ic pul­monary fi­bro­sis and lo­cal­ly ad­vanced pan­cre­at­ic can­cer. On Fri­day, the San Fran­cis­co-based drug de­vel­op­er un­veiled ear­ly da­ta from a small, sin­gle arm study at the Par­ent Project Mus­cu­lar Dy­s­tro­phy con­fer­ence in Or­lan­do, Flori­da.

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