Jay Bradner (Jeff Rumans for Endpoints News)

No­var­tis part­ners with the Gates Foun­da­tion on one of the Holy Grails in gene ther­a­py: a sim­ple, in vi­vo ap­proach to cur­ing sick­le cell dis­ease

Hav­ing helped ush­er in a “new era” of sick­le cell dis­ease treat­ment with Adakveo, No­var­tis has set its sights on an even high­er goal: a cu­ra­tive, rel­a­tive­ly low cost, once-and-done in vi­vo gene ther­a­py that can work in de­vel­op­ing coun­tries.

Tap­ping in­to the cof­fers of the Bill & Melin­da Gates Foun­da­tion, the phar­ma gi­ant says it will de­ploy its drug dis­cov­ery and gene ther­a­py ex­perts in search of a prod­uct that can cater to re­gions with less re­sources. And they’re us­ing to­day’s an­nounce­ment to open its doors to any oth­er groups that would like to pitch in.

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