Roche un­corks new long-term da­ta as SMA ri­val­ry heats up

Lead­ing up to a reg­u­la­to­ry de­ci­sion in May that could give Roche a big leg up on Bio­gen and No­var­tis in the spinal mus­cu­lar at­ro­phy space, the Swiss phar­ma gi­ant is hop­ing some new da­ta will bol­ster its case.

Roche un­corked some long-term ef­fi­ca­cy and safe­ty da­ta for its block­buster SMA drug Evrys­di (ris­diplam) on Wednes­day, while al­so of­fer­ing an­oth­er peek at the in­ter­im re­sults for its RAIN­BOW­FISH study in new­borns un­der 2 months old.

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