Sarep­ta halts its golodirsen Duchenne MD study in UK af­ter pa­tient ex­pe­ri­ences ad­verse event

Sarep­ta said this morn­ing that it has halt­ed dos­ing its Duchenne mus­cu­lar dy­s­tro­phy drug golodirsen at all its UK sites af­ter one of the pa­tients in the tri­al ex­pe­ri­enced an ad­verse event. But the biotech swift­ly in­di­cat­ed that it doesn’t ex­pect the halt to last for long.

The news was first re­port­ed by EP Van­tage writer Ja­cob Pli­eth, who not­ed chat­ter about the dos­ing halt on Face­book cit­ing is­sues with rhab­domy­ol­y­sis side ef­fects — a break­down of mus­cle tis­sue that trig­gers se­vere pain.

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