Doug Ingram, Sarepta CEO

Sarep­ta's sec­ond shot at show­ing its Duchenne gene ther­a­py de­liv­ers pos­i­tive da­ta but un­der­whelms — shares tum­ble

When Sarep­ta re­vealed last Jan­u­ary that its gene ther­a­py for Duchenne mus­cu­lar dy­s­tro­phy had failed the key func­tion­al end­point in Part 1 of a Phase II tri­al, ex­ec­u­tives un­der­scored that there’s a sec­ond part to the study — giv­ing them an­oth­er shot at a fa­vor­able read­out.

One year lat­er, Sarep­ta is tak­ing the vir­tu­al podi­um at JP Mor­gan to present what they call pos­i­tive re­sults.

But re­ac­tions are de­cid­ed­ly mixed, and in­vestors sent shares $SRPT tum­bling 10.94% to $76.15.

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