Sol­id Bio’s high­er gene ther­a­py dose for Duchenne MD runs smack in­to a fresh set of safe­ty is­sues -- shares tum­ble

Sol­id Bio­sciences has just ric­o­cheted in­to a new set­back.A few months af­ter re­port­ing dis­mal re­spons­es from a small co­hort of pa­tients re­ceiv­ing its gene ther­a­py for Duchenne mus­cu­lar dy­s­tro­phy, the biotech had a chance to in­crease the dose to what it felt would be an ide­al lev­el — and im­me­di­ate­ly ran in­to a se­ri­ous ad­verse event that had to be re­port­ed to the FDA.

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