There has to be a better way to handle Duchenne drugs; Let's get to the bottom of the Juno debacle
Endpoints assesses the big biopharma R&D stories of the week, with a little added commentary on what they mean for the industry.
Long after it became apparent that PTC’s Duchenne drug doesn’t work, the EMA’s green light is intact
I never understood why the EMA would suddenly reverse itself in 2014 and allow PTC to sell ataluren as its only approved therapy on the continent for Duchenne muscular dystrophy. And it was even more perplexing to see the European regulator come back last year and decide to allow the drug to remain on the market as PTC lined up a new late-stage study over an expansive 5-year grace period.
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