Ul­tragenyx shares tum­ble low­er af­ter rare dis­ease drug fails PhII tri­al

Shares of Ul­tragenyx $RARE tum­bled close to 10% af­ter the rare dis­ease biotech re­port­ed that one of its drugs failed a Phase II tri­al.

UX007 was test­ed as a treat­ment for glu­cose trans­porter type-1 de­fi­cien­cy syn­drome—or Glut1 DS—among a small group of pa­tients. But it on­ly cut the rate of seizures in the drug arm by 13.4% com­pared to the place­bo arm, falling short of sta­tis­ti­cal sig­nif­i­cance.

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