Ultragenyx shares tumble lower after rare disease drug fails PhII trial
Shares of Ultragenyx $RARE tumbled close to 10% after the rare disease biotech reported that one of its drugs failed a Phase II trial.
UX007 was tested as a treatment for glucose transporter type-1 deficiency syndrome—or Glut1 DS—among a small group of patients. But it only cut the rate of seizures in the drug arm by 13.4% compared to the placebo arm, falling short of statistical significance.
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