June 17, 2020 10:30 AM EDT
R&D
Cell/Gene Tx

Bio­Marin spells out a trou­bling slide in Fac­tor VI­II lev­els for its big block­buster con­tender val­rox

John Carroll

Editor & Founder

We al­ready knew from Bio­Marin’s state­ment a few days ago that their gene ther­a­py for he­mo­phil­ia A con­tin­ued to pro­tect pa­tients against the bleed­ing …

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