Recently stung by AAV, Sarepta dives a little deeper into non-viral delivery with newest licensing pact

Kyle Blankenship

The use of adeno-associated viruses (AAV) as delivery vehicles for gene therapeutics has been riddled with safety concerns for years — a fact Sarepta knows well …

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Recently stung by AAV, Sarepta dives a little deeper into non-viral delivery with newest licensing pact

Kyle Blankenship

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Applied Therapeutics' rare disease drug gets a CRL

FDA is looking into hematology risks after patients take Bluebird's Skysona gene therapy

Novartis to cut 139 jobs in NJ as part of commercial refocus

PTC reports Phase 2 ALS fail, sells priority review voucher for $150M

To lead NIH, Trump taps Stanford academic and pandemic response critic Jay Bhattacharya

Advanz Pharma faces revocation of European authorization for liver disease drug Ocaliva

Re­cent­ly stung by AAV, Sarep­ta dives a lit­tle deep­er in­to non-vi­ral de­liv­ery with newest li­cens­ing pact

Kyle Blankenship

Sign up to read this article for free.

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Recently stung by AAV, Sarepta dives a little deeper into non-viral delivery with newest licensing pact

Applied Therapeutics' rare disease drug gets a CRL

FDA is looking into hematology risks after patients take Bluebird's Skysona gene therapy

Novartis to cut 139 jobs in NJ as part of commercial refocus

PTC reports Phase 2 ALS fail, sells priority review voucher for $150M

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Advanz Pharma faces revocation of European authorization for liver disease drug Ocaliva