First clin­i­cal test of RNA edit­ing re­stores miss­ing pro­tein in ge­net­ic dis­ease, Wave says

An ex­per­i­men­tal ther­a­py de­signed to change a sin­gle let­ter of short-lived mR­NA mol­e­cules has cor­rect­ed a ge­net­ic mu­ta­tion that pre­vents peo­ple from mak­ing a vi­tal …

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