Ap­plied Ther­a­peu­tic­s' rare dis­ease drug gets a CRL

The FDA re­ject­ed Ap­plied Ther­a­peu­tics’ ex­per­i­men­tal treat­ment for a rare dis­ease called clas­sic galac­tosemia, cit­ing de­fi­cien­cies with the ap­pli­ca­tion.

The com­pa­ny, while “dis­ap­point­ed with the …

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