October 5, 2017 07:03 AM EDTUpdated May 26, 08:50 PM

Bluebird’s gene therapy shows promise in keeping lethal Lorenzo’s Oil disease in check

John Carroll

Editor & Founder

After an average of 29 months following a one-time gene therapy infusion, a clear majority of boys suffering from lethal cases of cerebral adrenoleukodystrophy were …

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Bluebird’s gene therapy shows promise in keeping lethal Lorenzo’s Oil disease in check

John Carroll

Editor & Founder

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Blue­bird’s gene ther­a­py shows promise in keep­ing lethal Loren­zo’s Oil dis­ease in check

John Carroll

Editor & Founder

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Bluebird’s gene therapy shows promise in keeping lethal Lorenzo’s Oil disease in check

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Novartis to cut 139 jobs in NJ as part of commercial refocus

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Advanz Pharma faces revocation of European authorization for liver disease drug Ocaliva

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