Agios’ Pyrukynd suc­ceeds in key tri­al of rare red blood cell dis­or­der in kids

Agios’ blood dis­ease treat­ment Pyrukynd passed a Phase 3 study in PK de­fi­cien­cy in chil­dren who do not reg­u­lar­ly re­ceive blood trans­fu­sions.

The read­out ar­rives …

Endpoints News

Sign up to read this article for free.

Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.