Applied Therapeutics says rare disease drug fails PhIII trial, still plans to seek approval

Paul Schloesser

Associate Editor

Applied Therapeutics, which is developing a treatment for a rare disease that affects children who can’t process a sugar called galactose, missed the primary endpoint …

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Applied Therapeutics says rare disease drug fails PhIII trial, still plans to seek approval

Paul Schloesser

Associate Editor

Sign up to read this article for free.

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