Astel­las de­tails po­ten­tial rea­son be­hind deaths in rare dis­ease gene ther­a­py tri­al

Four boys with a rare and of­ten se­vere ge­net­ic mus­cle dis­ease died in 2020 and 2021 af­ter re­ceiv­ing a one-time gene ther­a­py from Astel­las Phar­ma …

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