As cash runs tight, blue­bird plunges af­ter pric­ing sick­le cell gene ther­a­py well above com­peti­tor and fail­ing to win re­view vouch­er

In­vestors re­act­ed neg­a­tive­ly to blue­bird bio’s pric­ing plans for its new sick­le cell ther­a­py, as well as the lack of a valu­able pri­or­i­ty re­view vouch­er and black box warn­ing for the treat­ment.

Fri­day’s FDA ap­proval of blue­bird’s Lyf­ge­nia came two weeks ahead of sched­ule and on the same day Ver­tex Phar­ma­ceu­ti­cals and CRISPR Ther­a­peu­tics land­ed a his­toric clear­ance for Cas­gevy, their CRISPR-based med­i­cine for the same dis­ease.

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