Emmaus who? A biotech you never heard of just won an historic drug OK for sickle cell disease
After pursuing an R&D odyssey that stretched out more than 15 years, little Emmaus Life Sciences in Torrance, CA has just won an FDA OK for Endari, the first new drug approved for sickle cell disease in close to 20 years.
Operated by Yutaka Niihara, Emmaus gained the backing of a large majority of outside experts brought in by the agency to review the drug. “Until now, only one other drug was approved for patients living with this serious, debilitating condition,” noted the FDA’s Richard Pazdur in marking the OK.
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