Bobby Gaspar, Orchard Therapeutics CEO
March 18, 2024 02:59 PM EDTUpdated 04:55 PM
Pharma
Cell/Gene Tx
FDA+

FDA green­lights Or­chard's gene ther­a­py Len­meldy for rare and fa­tal dis­ease

Lei Lei Wu

News Reporter

The FDA ap­proved a gene ther­a­py known as Len­meldy for ear­ly-on­set metachro­mat­ic leukody­s­tro­phy, or MLD, a rare and fa­tal ge­net­ic dis­ease …

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