FDA of­fers first thoughts on neu­rode­gen­er­a­tive dis­ease gene ther­a­pies

The FDA has is­sued draft guid­ance on the de­vel­op­ment, test­ing, and tri­al de­sign for hu­man gene ther­a­pies for neu­rode­gen­er­a­tive dis­eases. The doc­u­ment, re­leased on Tues­day …

Sign up to read this article for free.

Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.

SIGN UP LOG IN BECOME A PREMIUM SUBSCRIBER