Peter Marks (AP Photo/Susan Walsh, Pool)

FDA's Pe­ter Marks lays out plans to sup­port gene ther­a­pies for ul­tra-rare dis­eases

It’s rare to hear an FDA leader say that the use of ran­dom­ized con­trolled tri­als “bor­ders on the ab­surd.”

But that’s what CBER di­rec­tor Pe­ter …

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