Photo: Lei Lei Wu for Endpoints News
May 9, 2024 09:38 AM EDT
R&D
Cell/Gene Tx

Free­line un­veils ear­ly ef­fi­ca­cy sig­nal for Gauch­er gene ther­a­py: #AS­GCT24

Lei Lei Wu

News Reporter

BAL­TI­MORE — Four pa­tients with Gauch­er dis­ease were able to stop their reg­u­lar treat­ments af­ter re­ceiv­ing a one-time in­fu­sion of a gene ther­a­py de­vel­oped by Free­line …

Endpoints News

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