Photo: Lei Lei Wu for Endpoints News
Freeline unveils early efficacy signal for Gaucher gene therapy: #ASGCT24
BALTIMORE — Four patients with Gaucher disease were able to stop their regular treatments after receiving a one-time infusion of a gene therapy developed by Freeline …
Sign up to read this article for free.
Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.