Is Spin­raza worth $750K? Bio­gen says yes, spelling out re­duced death risk

Bio­gen took a lot of an­a­lysts by sur­prise re­cent­ly when the big biotech an­nounced that its break­through drug for spinal mus­cu­lar at­ro­phy would be priced at $750,000 for the first year, and $375,000 for each sub­se­quent year. But in­ves­ti­ga­tors just spelled out the da­ta from their piv­otal study, demon­strat­ing a clear re­duc­tion in the risk of death.

While the study was stopped ear­ly due to its suc­cess, 68% of the un­treat­ed in­fants in the study ei­ther died or re­quired per­ma­nent ven­ti­la­tion com­pared to 39% of the drug arm. That rep­re­sent­ed a 47% drop in the risk of death or need for per­ma­nent ven­ti­la­tion.

Endpoints News

Unlock this article instantly by becoming a free subscriber.

You’ll get access to free articles each month, plus you can customize what newsletters get delivered to your inbox each week, including breaking news.