Exclusive: Jnana says pivotal trial of PKU pill could begin next year after promising results from a smaller study
Jnana Therapeutics, a Boston startup that’s looking to tackle a rare metabolic disease, has reported promising results from an ongoing early clinical trial, giving it line-of-sight to jump straight into a pivotal study in 2025, the company told Endpoints News in an interview.
The study tested a twice-daily pill in adults with phenylketonuria, or PKU, an inherited disease that leaves people unable to break down a protein building block called phenylalanine.
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