CBER Director Peter Marks (Jim Lo Scalzo/Pool via AP Images)
November 27, 2023 03:11 PM EST
Cell/Gene Tx
FDA+

Marks: FDA open to us­ing sin­gle-arm stud­ies for ac­cel­er­at­ed ap­proval of rare dis­ease gene ther­a­pies

Lei Lei Wu

News Reporter

Pe­ter Marks, the FDA of­fi­cial who over­sees gene ther­a­pies, is again ad­vo­cat­ing for the use of ac­cel­er­at­ed ap­provals for gene ther­a­pies that …

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