Reenie McCarthy, Stealth BioTherapeutics CEO

Rare dis­ease drug­mak­er files for ap­proval de­spite ob­jec­tions from FDA on ad­e­quate tri­al da­ta

An­oth­er small biotech at­tack­ing a su­per-rare dis­ease is lever­ag­ing a pa­tient com­mu­ni­ty and very lim­it­ed clin­i­cal da­ta to try to win an FDA ap­proval. …

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