Sarepta gene therapy for Duchenne muscular dystrophy fails on function — raising serious questions about all their drugs
Sarepta $SRPT has some explaining to do.
After the market closed on Thursday the controversial biotech company reported that their next-gen gene therapy approach to Duchenne muscular dystrophy did what it was supposed to do in spurring a significant increase in dystrophin production, but failed on the key endpoint that aimed to demonstrate improved muscle function for the boys afflicted with this lethal condition.
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