Scoop: Inspired by the late Tachi Yamada, Jim Wilson launches new nonprofit targeting underserved ultra-rare diseases
A group of powerhouse biotech leaders is coming together to launch a new nonprofit, one aimed at delivering therapies to rare disease populations they believe pharma is leaving behind.
Jim Wilson, the famed gene therapy researcher, teamed up with the late Tachi Yamada and Braidwell’s Alex Karnal to launch the Institute for Life Changing Medicines. The institute, which officially debuts Thursday morning, will hit the ground running with a program for the ultra-rare Crigler-Najjar syndrome, planning to launch a first-in-human study later this year.
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