Scoop: In­spired by the late Tachi Ya­ma­da, Jim Wil­son launch­es new non­prof­it tar­get­ing un­der­served ul­tra-rare dis­eases

A group of pow­er­house biotech lead­ers is com­ing to­geth­er to launch a new non­prof­it, one aimed at de­liv­er­ing ther­a­pies to rare dis­ease pop­u­la­tions they be­lieve phar­ma is leav­ing be­hind.

Jim Wil­son, the famed gene ther­a­py re­searcher, teamed up with the late Tachi Ya­ma­da and Braid­well’s Alex Kar­nal to launch the In­sti­tute for Life Chang­ing Med­i­cines. The in­sti­tute, which of­fi­cial­ly de­buts Thurs­day morn­ing, will hit the ground run­ning with a pro­gram for the ul­tra-rare Crigler-Na­j­jar syn­drome, plan­ning to launch a first-in-hu­man study lat­er this year.

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