From L-R: Gerard Caelles, Miquel Vila-Perelló and Silvia Frutos (SpliceBio)

Some genes are too large to fit in­to AAV vec­tors. UCB, No­var­tis back $57M idea to de­liv­er them in parts in­stead

Of all the ma­jor lim­i­ta­tions of ade­no-as­so­ci­at­ed virus­es (AAV) as a vec­tor for gene ther­a­py, one is par­tic­u­lar­ly well-known and in­dis­putable: They can on­ly car­ry …

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