Some genes are too large to fit into AAV vectors. UCB, Novartis back $57M idea to deliver them in parts instead

Amber Tong

Of all the major limitations of adeno-associated viruses (AAV) as a vector for gene therapy, one is particularly well-known and indisputable: They can only carry …

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Some genes are too large to fit into AAV vectors. UCB, Novartis back $57M idea to deliver them in parts instead

Amber Tong

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Some genes are too large to fit in­to AAV vec­tors. UCB, No­var­tis back $57M idea to de­liv­er them in parts in­stead

Amber Tong

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