Still reel­ing from re­jec­tion, Bio­Marin re­ports a glimpse of those 2-year val­rox da­ta FDA was look­ing for — but is it enough to change reg­u­la­tors' minds?

Bio­Marin now has the Phase III da­ta it needs to re­file val­rox, its gene ther­a­py for he­mo­phil­ia A, at the EMA — and pos­si­bly con­vince the …

Endpoints News

Sign up to read this article for free.

Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.