Stuck with a PhI­II gene ther­a­py fail­ure at 96 weeks, Gen­Sight prefers the up­beat as­sess­ment

Two years af­ter treat­ment, the best thing that Gen­Sight Bi­o­log­ics $SIGHT can say about their gene ther­a­py for vi­sion-de­stroy­ing cas­es of Leber Hered­i­tary Op­tic Neu­ropa­thy is that it’s just a bit bet­ter than a place­bo — just maybe be­cause one treat­ment can cov­er both eyes.

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