Matt Kapusta, uniQure CEO (via website)

The FDA slaps a hold on uniQure's he­mo­phil­ia B gene ther­a­py as re­searchers ex­plore a case of liv­er can­cer in lat­est set­back for a boom­ing field

In the lat­est sam­pling of a set­back in the stum­ble-prone gene ther­a­py field, uniQure to­day an­nounced that the FDA has slapped a clin­i­cal hold on its work re­gard­ing their all-im­por­tant he­mo­phil­ia B pro­gram af­ter a pa­tient in the study de­vel­oped liv­er can­cer.

The stock $QURE, which hinges on the fate of uniQure’s piv­otal study for etranaco­gene deza­parvovec, slid more than 20% ahead of the bell on Mon­day.

Endpoints News

Unlock this article instantly by becoming a free subscriber.

You’ll get access to free articles each month, plus you can customize what newsletters get delivered to your inbox each week, including breaking news.