The FDA slaps a hold on uniQure's hemophilia B gene therapy as researchers explore a case of liver cancer in latest setback for a booming field
In the latest sampling of a setback in the stumble-prone gene therapy field, uniQure today announced that the FDA has slapped a clinical hold on its work regarding their all-important hemophilia B program after a patient in the study developed liver cancer.
The stock $QURE, which hinges on the fate of uniQure’s pivotal study for etranacogene dezaparvovec, slid more than 20% ahead of the bell on Monday.
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