April 15, 2024 11:14 AM EDT
R&D

Ul­tragenyx preps for piv­otal tri­al in An­gel­man syn­drome, an area where oth­ers fell short: #AAN24

Max Gelman

Senior Editor

Ul­tragenyx is inch­ing clos­er to a Phase 3 study for its An­gel­man syn­drome pro­gram, known as GTX-102.

In a Phase 1/2 up­date Mon­day morn­ing ahead …

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