UniQure unveils mixed Huntington's gene therapy data, shares tank
UniQure shared updated data from a Phase I/II study that showed a clinical benefit in a small group of patients with Huntington’s disease who received its gene therapy, but conflicting data about the mutant Huntingtin protein sent shares $QURE down by about 40% on Wednesday morning.
The Dutch biotech on Wednesday revealed new data from the placebo-controlled Phase I/II study with 26 patients. Sixteen patients were given a low or high dose of AMT-130, with 10 patients in the control group.
Unlock this article instantly by becoming a free subscriber.
You’ll get access to free articles each month, plus you can customize what newsletters get delivered to your inbox each week, including breaking news.