Vertex and CRISPR spotlight another important gene editing advance in a march to a hoped-for cure

John Carroll

Editor & Founder

Vertex and CRISPR Therapeutics have successfully navigated another stretch of the maiden clinical journey of the gene editing therapy CTX001 in a tiny group of …

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Vertex and CRISPR spotlight another important gene editing advance in a march to a hoped-for cure

John Carroll

Editor & Founder

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Applied Therapeutics' rare disease drug gets a CRL

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FDA is looking into hematology risks after patients take Bluebird's Skysona gene therapy

Norbert Bischofberger's time as Kronos CEO ends as biotech seeks new life

Novartis to cut 139 jobs in NJ as part of commercial refocus

Bristol Myers sues the federal government over 340B, following other drugmakers

Ver­tex and CRISPR spot­light an­oth­er im­por­tant gene edit­ing ad­vance in a march to a hoped-for cure

John Carroll

Editor & Founder

Sign up to read this article for free.

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