With ‘break­through’ sta­tus and a handy nick­name, Bio­Marin plots speedy PhI­II for gene ther­a­py

The FDA has hand­ed out its break­through ther­a­py des­ig­na­tion for Bio­Marin’s close­ly-watched gene ther­a­py drug BMN 270 for he­mo­phil­ia A.

In their Q3 call on …

Endpoints News

Sign up to read this article for free.

Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.