With new pivotal data, uniQure and CSL Behring dash to the FDA with a potential blockbuster gene therapy for hemophilia B

Nicole DeFeudis

Editor

After a five-month hold put a damper on uniQure’s hemophilia B gene therapy program, things are finally looking up as a positive pivotal readout puts …

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With new pivotal data, uniQure and CSL Behring dash to the FDA with a potential blockbuster gene therapy for hemophilia B

Nicole DeFeudis

Editor

Sign up to read this article for free.

Merck buys into PD-1/VEGF space as Summit comes for Keytruda

BeiGene will rebrand to BeOne Medicines, dropping name's link to China roots

As bluebird projects more commercial demand, the biotech continues to seek cash

Exclusive: Ascidian CEO Michael Ehlers leaves Apple Tree Partners for MPM BioImpact

FDA approves PTC’s ultra-rare disease gene therapy for broader patient population than Europe

What Will It Take to Reverse Fibrosis in Patients with Advanced MASH?

With new piv­otal da­ta, uniQure and CSL Behring dash to the FDA with a po­ten­tial block­buster gene ther­a­py for he­mo­phil­ia B

Nicole DeFeudis

Editor

Sign up to read this article for free.

Mer­ck buys in­to PD-1/VEGF space as Sum­mit comes for Keytru­da

BeiGene will re­brand to BeOne Med­i­cines, drop­ping name's link to Chi­na roots

As blue­bird projects more com­mer­cial de­mand, the biotech con­tin­ues to seek cash

Ex­clu­sive: As­cid­i­an CEO Michael Ehlers leaves Ap­ple Tree Part­ners for MPM BioIm­pact

FDA ap­proves PTC’s ul­tra-rare dis­ease gene ther­a­py for broad­er pa­tient pop­u­la­tion than Eu­rope

What Will It Take to Re­verse Fi­bro­sis in Pa­tients with Ad­vanced MASH?

With new pivotal data, uniQure and CSL Behring dash to the FDA with a potential blockbuster gene therapy for hemophilia B

Merck buys into PD-1/VEGF space as Summit comes for Keytruda

BeiGene will rebrand to BeOne Medicines, dropping name's link to China roots

As bluebird projects more commercial demand, the biotech continues to seek cash

Exclusive: Ascidian CEO Michael Ehlers leaves Apple Tree Partners for MPM BioImpact

FDA approves PTC’s ultra-rare disease gene therapy for broader patient population than Europe

What Will It Take to Reverse Fibrosis in Patients with Advanced MASH?