As CRISPR emerges, re­searchers spot­light pos­i­tive ef­fects in pre­na­tal gene edit­ing treat­ment for mice

In a break­through for the buzzing world of CRISPR re­search, a team of sci­en­tists has demon­strat­ed a use of the gene edit­ing tool to treat a ge­net­ic dis­ease in mice be­fore they are born.

The proof-of-con­cept study brings them one step clos­er — though still miles away — to the ul­ti­mate goal of treat­ing se­vere hu­man dis­eases di­ag­nosed ear­ly in preg­nan­cy, ac­cord­ing to the re­searchers from Chil­dren’s Hos­pi­tal of Philadel­phia and the Perel­man School of Med­i­cine at the Uni­ver­si­ty of Penn­syl­va­nia.

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