April 12, 2018 09:59 AM EDT
News Briefing

Pfiz­er launch­es a gene ther­a­py study for Duchenne MD; Am­gen, NEA back re­al-world drug da­ta soft­ware com­pa­ny

John Carroll

Editor & Founder

→ Pfiz­er has launched its close­ly-watched study of a new “mi­ni-dy­s­trophin” gene ther­a­py for Duchenne mus­cu­lar dy­s­tro­phy. Duke’s Ed­ward Smith dosed the first boy …

Endpoints News

Sign up to read this article for free.

Get free access to a limited number of articles, plus choose newsletters to get straight to your inbox.

BECOME A PREMIUM SUBSCRIBER
TRENDING NOW

Lil­ly’s oral SERD makes strides in breast can­cer with Phase 3 da­ta

The End­points 100: The biotech in­dus­try braces for Trump 2.0

Ex­clu­sive: Bain-backed mus­cu­loskele­tal biotech rais­es $120M for trio of clin­i­cal-stage bi­o­log­ics

Ace­lyrin says good­bye to the drug that got it a $540M IPO in 2023

Gene edit­ing com­pa­nies seek safer, less gru­el­ing con­di­tion­ing meth­ods for blood stem cell ther­a­pies

sponsored

The key to faster, more im­pact­ful re­search? Put pa­tients in the dri­ver’s seat

A service from the Financial Times