February 12, 2020 10:34 AM EST
News Briefing

Pre­vail's gene ther­a­py scores or­phan, rare pe­di­atric dis­ease priv­i­leges; Ger­many's ITM se­cures €40M loan

Amber Tong

→ Pre­vail Ther­a­peu­tics’ gene ther­a­py for Gauch­er dis­ease now has both or­phan drug and rare pe­di­atric dis­ease des­ig­na­tions from the …

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